Empowered Patient Podcast
Gene Silencing Driving Drug Development for Rare Diseases with Dietrich Stephan NeuBase Therapeutics
- Author: Vários
- Narrator: Vários
- Publisher: Podcast
- Duration: 0:17:14
- More information
Informações:
Synopsis
Dietrich Stephan PhD, CEO, NeuBase Therapeutics discusses the history of research into the genetic basis of all diseases, NeuBase's PATrOL™ platform allowing for intelligent design of drugs that engage with a malfunctioning gene, and the company's therapies in development for Huntington's disease and myotonic dystrophy, which Dr. Stephan describes as "heat seeking missiles" because they are so specific and targeted to the broken gene of interest. @NeuBaseinc #RareDisease #GeneSilencing #HuntingtonsDisease #DM1 $NBSE NeuBaseTherapeutics.com Download the transcript here.